Q1 2025 Holdings
Filed 2025-05-15 | 44 holdings | $525.1M | 13F-HR | View on SEC ↗ · Holdings Table ↗
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| Issuer | Class | CUSIP | Value ↓ | Shares | % Portfolio |
|---|---|---|---|---|---|
| Insmed Inc(INSM) | COM PAR $.01 | 457669307 | $75.3M | 987,153 | 14.3% |
| Biomarin Pharmaceutical Inc(BMRN) | COM | 09061G101 | $70.1M | 991,207 | 13.3% |
| Amicus Therapeutics Inc(FOLD) | COM | 03152W109 | $59.9M | 7,345,002 | 11.4% |
| Acadia Pharmaceuticals Inc(ACAD) | COM | 004225108 | $44.2M | 2,663,925 | 8.4% |
| United Therapeutics Corp(UTHR) | COM | 91307C102 | $32.4M | 105,228 | 6.2% |
| Biogen Inc(BIIB) | COM | 09062X103 | $28.0M | 204,923 | 5.3% |
| Alnylam Pharmaceuticals Inc(ALNY) | COM | 02043Q107 | $22.5M | 83,488 | 4.3% |
| PTC Therapeutics Inc(PTCT) | COM | 69366J200 | $20.6M | 404,196 | 3.9% |
| Prothena Corp PLC(PRTA) | SHS | G72800108 | $20.5M | 1,659,734 | 3.9% |
| Anaptysbio Inc(ANAB) | COM | 032724106 | $19.0M | 1,020,713 | 3.6% |
| Novocure LTD(NVCR) | ORD SHS | G6674U108 | $17.9M | 1,002,061 | 3.4% |
| Sarepta Therapeutics Inc(SRPT) | COM | 803607100 | $13.4M | 210,258 | 2.6% |
| Ehealth Inc(EHTH) | COM | 28238P109 | $11.3M | 1,684,336 | 2.1% |
| Iovance Biotherapeutics Inc(IOVA) | COM | 462260100 | $10.7M | 3,211,314 | 2.0% |
| Staar Surgical Co(STAA) | COM PAR $0.01 | 852312305 | $9.3M | 525,017 | 1.8% |
| Agios Pharmaceuticals Inc(AGIO) | COM | 00847X104 | $8.1M | 276,578 | 1.5% |
| Alkermes PLC(ALKS) | SHS | G01767105 | $7.3M | 221,513 | 1.4% |
| Gossamer BIO Inc(GOSS) | COM | 38341P102 | $6.9M | 6,276,893 | 1.3% |
| Align Technology Inc(ALGN) | COM | 016255101 | $6.0M | 37,772 | 1.1% |
| Syndax Pharmaceuticals Inc(SNDX) | COM | 87164F105 | $5.5M | 444,367 | 1.0% |
| Acelyrin Inc | COM | 00445A100 | $4.4M | 1,792,895 | 0.8% |
| Dyne Therapeutics Inc(DYN) | COM | 26818M108 | $3.5M | 333,391 | 0.7% |
| Mirum Pharmaceuticals Inc(MIRM) | COM | 604749101 | $2.9M | 64,700 | 0.6% |
| Edwards Lifesciences Corp(EW) | COM | 28176E108 | $2.9M | 39,473 | 0.5% |
| Verve Therapeutics Inc | COM | 92539P101 | $2.6M | 575,817 | 0.5% |
| Biontech SE(BNTX) | SPONSORED ADS | 09075V102 | $2.3M | 25,206 | 0.4% |
| Bicycle Therapeutics PLC(BCYC) | SPONSORED ADS | 088786108 | $2.1M | 248,934 | 0.4% |
| Travere Therapeutics Inc(TVTX) | COM | 89422G107 | $2.0M | 110,719 | 0.4% |
| Taysha Gene Therapies Inc(TSHA) | COM SHS | 877619106 | $2.0M | 1,419,468 | 0.4% |
| Neurocrine Biosciences Inc(NBIX) | COM | 64125C109 | $1.5M | 13,334 | 0.3% |
| Nuvation BIO Inc(NUVB) | COM CL A | 67080N101 | $1.4M | 772,652 | 0.3% |
| Aldeyra Therapeutics Inc(ALDX) | COM | 01438T106 | $1.3M | 225,465 | 0.2% |
| Karyopharm Therapeutics Inc(KPTIEUR) | COM | 48576U106 | $1.2M | 324,032 | 0.2% |
| Aclaris Therapeutics Inc(ACRS) | COM | 00461U105 | $1.2M | 776,028 | 0.2% |
| Humana Inc(HUM) | COM | 444859102 | $1.1M | 3,985 | 0.2% |
| Pyxis Oncology Inc(PYXS) | COMMON STOCK | 747324101 | $1.0M | 1,037,421 | 0.2% |
| Stoke Therapeutics Inc(STOK) | COM | 86150R107 | $837.0K | 125,861 | 0.2% |
| Vyne Therapeutics Inc Pipe(VYNE) | COM | 92941V308 | $703.8K | 445,434 | 0.1% |
| Abeona Therapeutics Inc(ABEO) | COM NEW | 00289Y206 | $518.2K | 108,865 | 0.1% |
| Urogen Pharma LTD(URGN) | COM | M96088105 | $271.0K | 24,500 | 0.1% |
| Instil BIO Inc(TIL) | COM NEW | 45783C200 | $193.8K | 11,165 | 0.0% |
| Akari Therapeutics PLC(AKTX) | SPONSORED ADR | 00972G207 | $181.1K | 146,024 | 0.0% |
| Relmada Therapeutics Inc(RLMD) | COM | 75955J402 | $133.7K | 495,146 | 0.0% |
| Generation BIO Co(GBIOGBX) | COM | 37148K100 | $60.9K | 150,475 | 0.0% |