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Palo Alto Investors LP

Q1 2025 Holdings

Filed 2025-05-15 | 44 holdings | $525.1M | 13F-HR | View on SEC ↗ · Holdings Table ↗

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IssuerClassCUSIPValue ↓Shares% Portfolio
Insmed Inc(INSM)COM PAR $.01457669307$75.3M987,15314.3%
Biomarin Pharmaceutical Inc(BMRN)COM09061G101$70.1M991,20713.3%
Amicus Therapeutics Inc(FOLD)COM03152W109$59.9M7,345,00211.4%
Acadia Pharmaceuticals Inc(ACAD)COM004225108$44.2M2,663,9258.4%
United Therapeutics Corp(UTHR)COM91307C102$32.4M105,2286.2%
Biogen Inc(BIIB)COM09062X103$28.0M204,9235.3%
Alnylam Pharmaceuticals Inc(ALNY)COM02043Q107$22.5M83,4884.3%
PTC Therapeutics Inc(PTCT)COM69366J200$20.6M404,1963.9%
Prothena Corp PLC(PRTA)SHSG72800108$20.5M1,659,7343.9%
Anaptysbio Inc(ANAB)COM032724106$19.0M1,020,7133.6%
Novocure LTD(NVCR)ORD SHSG6674U108$17.9M1,002,0613.4%
Sarepta Therapeutics Inc(SRPT)COM803607100$13.4M210,2582.6%
Ehealth Inc(EHTH)COM28238P109$11.3M1,684,3362.1%
Iovance Biotherapeutics Inc(IOVA)COM462260100$10.7M3,211,3142.0%
Staar Surgical Co(STAA)COM PAR $0.01852312305$9.3M525,0171.8%
Agios Pharmaceuticals Inc(AGIO)COM00847X104$8.1M276,5781.5%
Alkermes PLC(ALKS)SHSG01767105$7.3M221,5131.4%
Gossamer BIO Inc(GOSS)COM38341P102$6.9M6,276,8931.3%
Align Technology Inc(ALGN)COM016255101$6.0M37,7721.1%
Syndax Pharmaceuticals Inc(SNDX)COM87164F105$5.5M444,3671.0%
Acelyrin IncCOM00445A100$4.4M1,792,8950.8%
Dyne Therapeutics Inc(DYN)COM26818M108$3.5M333,3910.7%
Mirum Pharmaceuticals Inc(MIRM)COM604749101$2.9M64,7000.6%
Edwards Lifesciences Corp(EW)COM28176E108$2.9M39,4730.5%
Verve Therapeutics IncCOM92539P101$2.6M575,8170.5%
Biontech SE(BNTX)SPONSORED ADS09075V102$2.3M25,2060.4%
Bicycle Therapeutics PLC(BCYC)SPONSORED ADS088786108$2.1M248,9340.4%
Travere Therapeutics Inc(TVTX)COM89422G107$2.0M110,7190.4%
Taysha Gene Therapies Inc(TSHA)COM SHS877619106$2.0M1,419,4680.4%
Neurocrine Biosciences Inc(NBIX)COM64125C109$1.5M13,3340.3%
Nuvation BIO Inc(NUVB)COM CL A67080N101$1.4M772,6520.3%
Aldeyra Therapeutics Inc(ALDX)COM01438T106$1.3M225,4650.2%
Karyopharm Therapeutics Inc(KPTIEUR)COM48576U106$1.2M324,0320.2%
Aclaris Therapeutics Inc(ACRS)COM00461U105$1.2M776,0280.2%
Humana Inc(HUM)COM444859102$1.1M3,9850.2%
Pyxis Oncology Inc(PYXS)COMMON STOCK747324101$1.0M1,037,4210.2%
Stoke Therapeutics Inc(STOK)COM86150R107$837.0K125,8610.2%
Vyne Therapeutics Inc Pipe(VYNE)COM92941V308$703.8K445,4340.1%
Abeona Therapeutics Inc(ABEO)COM NEW00289Y206$518.2K108,8650.1%
Urogen Pharma LTD(URGN)COMM96088105$271.0K24,5000.1%
Instil BIO Inc(TIL)COM NEW45783C200$193.8K11,1650.0%
Akari Therapeutics PLC(AKTX)SPONSORED ADR00972G207$181.1K146,0240.0%
Relmada Therapeutics Inc(RLMD)COM75955J402$133.7K495,1460.0%
Generation BIO Co(GBIOGBX)COM37148K100$60.9K150,4750.0%