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Palo Alto Investors LP

Q3 2025 Holdings

Filed 2025-11-14 | 44 holdings | $540.4M | 13F-HR | View on SEC ↗ · Holdings Table ↗

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IssuerClassCUSIPValue ↓Shares% Portfolio
Insmed Inc(INSM)COM457669307$70.8M491,80513.1%
PTC Therapeutics Inc(PTCT)COM69366J200$52.9M862,6139.8%
Acadia Pharmaceuticals Inc(ACAD)COM004225108$52.6M2,466,6849.7%
Amicus Therapeutics Inc(FOLD)COM03152W109$42.3M5,367,7987.8%
Biomarin Pharmaceutical Inc(BMRN)COM09061G101$40.8M754,0077.6%
Biogen Inc(BIIB)SPONSORED ADS09062X103$26.0M185,6614.8%
United Therapeutics Corp(UTHR)COM91307C102$24.4M58,1864.5%
Anaptysbio Inc(ANAB)COM032724106$20.6M673,5203.8%
Iovance Biotherapeutics Inc(IOVA)COM NEW462260100$16.5M7,618,1323.1%
Novocure LTD(NVCR)COMG6674U108$16.2M1,256,1593.0%
Dyne Therapeutics Inc(DYN)SPONSORED ADS26818M108$16.0M1,262,6743.0%
Disc Medicine Inc(IRON)COM254604101$14.8M224,3002.7%
Alnylam Pharmaceuticals Inc(ALNY)COM02043Q107$14.7M32,3202.7%
Gossamer BIO Inc(GOSS)COM38341P102$14.4M5,464,3492.7%
Prothena Corp PLC(PRTA)COM CL AG72800108$12.9M1,324,0282.4%
Ultragenyx Pharmaceutical in(RARE)COM90400D108$11.1M369,5312.1%
Agios Pharmaceuticals Inc(AGIO)COM00847X104$10.7M265,4972.0%
Syndax Pharmaceuticals Inc(SNDX)COM87164F105$10.1M654,9301.9%
Ehealth Inc(EHTH)COM28238P109$6.7M1,544,6191.2%
Denali Therapeutics Inc(DNLI)COM24823R105$5.9M408,0061.1%
Align Technology Inc(ALGN)COM016255101$5.7M45,7351.1%
Alkermes PLC(ALKS)COMG01767105$5.5M183,9381.0%
Avidity Biosciences Inc(RNA)COM05370A108$4.8M109,8310.9%
Mirum Pharmaceuticals Inc(MIRM)COM604749101$4.7M64,7000.9%
Caredx Inc(CDNA)COM14167L103$4.6M316,2040.9%
Taysha Gene Therapies Inc(TSHA)COM877619106$4.1M1,246,0330.8%
Nuvation BIO Inc(NUVB)COM CL A67080N101$3.8M1,020,5470.7%
Aclaris Therapeutics Inc(ACRS)COM00461U105$3.0M1,566,8400.6%
Crispr Therapeutics AG(CRSP)NAMEN AKTH17182108$2.7M41,2260.5%
Travere Therapeutics Inc(TVTX)COM SHS89422G107$2.6M110,7190.5%
Edwards Lifesciences Corp(EW)COM28176E108$2.6M33,6400.5%
Neurocrine Biosciences Inc(NBIX)COM64125C109$2.5M18,1170.5%
Stoke Therapeutics Inc(STOK)COM86150R107$2.5M105,4270.5%
Pyxis Oncology Inc(PYXS)COM747324101$2.3M1,037,4210.4%
Biontech SE(BNTX)COM09075V102$1.9M19,6140.4%
Bicycle Therapeutics PLC(BCYC)COM088786108$1.7M221,0710.3%
Aldeyra Therapeutics Inc(ALDX)SPONSORED ADR01438T106$1.2M225,4650.2%
Humana Inc(HUM)COM444859102$1.0M3,9850.2%
Oruka Therapeutics Inc(ORKA)COM687604108$791.3K59,9850.1%
Abeona Therapeutics Inc(ABEO)COM NEW00289Y206$574.8K108,8650.1%
Urogen Pharma LTD(URGN)COMM96088105$488.8K24,5000.1%
Proqr Therapeutics NVSHS EURON71542109$402.2K188,8070.1%
Akari Therapeutics PLC(AKTX)COM00972G207$147.5K146,0240.0%
Generation BIO Co(GBIOGBX)COM37148K100$92.1K15,0470.0%