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Palo Alto Investors LP

Q1 2026 Holdings

Filed 2026-05-15 | 51 holdings | $653.9M | 13F-HR | View on SEC ↗ · Holdings Table ↗

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IssuerClassCUSIPValue ↓Shares% Portfolio
Insmed Inc(INSM)COM PAR $.01457669307$67.9M415,26910.4%
Acadia Pharmaceuticals Inc(ACAD)COM004225108$63.9M2,872,6959.8%
PTC Therapeutics Inc(PTCT)COM69366J200$62.8M921,6079.6%
Biomarin Pharmaceutical Inc(BMRN)COM09061G101$38.7M685,1825.9%
United Therapeutics Corp(UTHR)COM91307C102$37.2M62,8095.7%
Anaptysbio Inc(ANAB)COM032724106$35.4M638,1615.4%
Mirum Pharmaceuticals Inc(MIRM)COM604749101$30.0M325,1754.6%
Dyne Therapeutics Inc(DYN)COM26818M108$30.0M1,652,9724.6%
Biogen Inc(BIIB)COM09062X103$25.8M140,7193.9%
Disc Medicine Inc(IRON)COM254604101$25.7M401,7193.9%
Iovance Biotherapeutics Inc(IOVA)COM462260100$22.3M6,349,5633.4%
Syndax Pharmaceuticals Inc(SNDX)COM87164F105$20.2M864,9863.1%
Annexon Inc(ANNX)COM03589W102$16.3M2,948,0902.5%
Amicus Therapeutics Inc(FOLD)COM03152W109$16.1M1,113,0452.5%
Novocure LTD(NVCR)ORD SHSG6674U108$14.0M1,280,4392.1%
Ultragenyx Pharmaceutical in(RARE)COM90400D108$12.5M596,4951.9%
Prothena Corp PLC(PRTA)SHSG72800108$11.7M1,208,5681.8%
Bicara Therapeutics Inc(BCAX)COM055477103$10.9M550,4081.7%
Celldex Therapeutics Inc(CLDX)COM NEW15117B202$9.4M296,4081.4%
Caredx Inc(CDNA)COM14167L103$9.2M531,8701.4%
Alkermes PLC(ALKS)SHSG01767105$8.6M242,5601.3%
Compass Therapeutics Inc(CMPX)COM20454B104$8.0M1,514,5041.2%
Agios Pharmaceuticals Inc(AGIO)COM00847X104$7.2M213,6011.1%
Align Technology Inc(ALGN)COM016255101$7.1M41,5201.1%
Capricor Therapeutics Inc(CAPR)COM NEW14070B309$7.0M229,7631.1%
Travere Therapeutics Inc(TVTX)COM89422G107$6.8M230,4531.0%
Taysha Gene Therapies Inc(TSHA)COM SHS877619106$6.2M1,391,3821.0%
Aclaris Therapeutics Inc(ACRS)COM00461U105$6.1M1,613,4300.9%
Denali Therapeutics Inc(DNLI)COM24823R105$4.5M234,5820.7%
Xenon Pharmaceuticals Inc(XENE)COM98420N105$3.0M51,3450.5%
Oruka Therapeutics Inc(ORKA)COM687604108$2.9M59,9850.5%
Stoke Therapeutics Inc(STOK)COM86150R107$2.8M84,6310.4%
Edwards Lifesciences Corp(EW)COM28176E108$2.7M33,6400.4%
Neurocrine Biosciences Inc(NBIX)COM64125C109$2.4M18,1170.4%
Nuvation BIO Inc(NUVB)COM CL A67080N101$2.2M508,8460.3%
Cytokinetics Inc(CYTK)COM NEW23282W605$2.1M32,1950.3%
Ehealth Inc(EHTH)COM28238P109$1.9M1,482,7970.3%
Crispr Therapeutics AG(CRSP)NAMEN AKTH17182108$1.9M39,6050.3%
Biontech SE(BNTX)SPONSORED ADS09075V102$1.7M19,6140.3%
Pyxis Oncology Inc(PYXS)COMMON STOCK747324101$1.5M1,010,5100.2%
Verastem Inc(VSTM)COM NEW92337C203$1.3M246,0930.2%
Bicycle Therapeutics PLC(BCYC)SPONSORED ADS088786108$936.8K201,8900.1%
Madrigal Pharmaceuticals Inc(MDGL)COM558868105$935.4K1,7870.1%
Humana Inc(HUM)COM444859102$691.0K3,9850.1%
Compass Pathways PLC ADR(CMPS)SPONSORED ADS20451W101$639.4K115,6160.1%
Xeris Biopharma Holdings Inc(XERS)COM98422E103$605.6K104,4100.1%
Abeona Therapeutics Inc(ABEO)COM NEW00289Y206$487.7K108,8650.1%
Inspire Medical Systems Inc(INSP)COM457730109$452.5K8,7720.1%
Urogen Pharma LTD(URGN)COMM96088105$440.5K24,5000.1%
Proqr Therapeutics NVSHS EURON71542109$305.9K188,8070.0%
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