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Palo Alto Investors LP

Q2 2026 Holdings

Filed 2026-08-17 | 52 holdings | $723.7M | 13F-HR/A | View on SEC ↗ · Holdings Table ↗

Amended (2026-08-19) | View on SEC ↗ · Holdings Table ↗

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IssuerClassCUSIPValue ↓Shares% Portfolio
PTC Therapeutics Inc(PTCT)COM69366J200$75.0M918,84610.4%
Acadia Pharmaceuticals Inc(ACHC)COM00404A109$72.5M2,864,09610.0%
Acadia Pharmaceuticals Inc(ACAD)ACOM004225108$72.5M2,864,09610.0%
Insmed Inc(INSM)COM PAR $.01457669307$44.1M413,9806.1%
Mirum Pharmaceuticals IncNOTE 4.000% 5/0604749AB7$40.8M$348,8085.6%
Mirum Pharmaceuticals Inc(MIRM)ACOM604749101$40.8M348,8085.6%
Anaptysbio Inc(ANAB)COM032724106$40.7M603,4895.6%
Biomarin Pharmaceutical Inc(BMRN)COM09061G101$39.1M682,7775.4%
Dyne Therapeutics Inc(DYN)COM26818M108$36.6M1,647,5215.1%
United Therapeutics Corp(UTHR)COM91307C102$33.9M62,5874.7%
Disc Medicine Inc(IRON)COM254604101$30.5M416,6464.2%
Biogen Inc(BIIB)COM09062X103$30.3M140,2794.2%
Iovance Biotherapeutics Inc(IOVA)COM462260100$22.0M5,296,2093.0%
Ultragenyx Pharmaceutical in(RARE)COM90400D108$19.9M596,4952.8%
Novocure LTD(NVCR)ORD SHSG6674U108$19.4M1,280,4392.7%
Syndax Pharmaceuticals Inc(SNDX)COM87164F105$18.9M864,9862.6%
Annexon Inc(ANNX)COM03589W102$16.8M2,948,0902.3%
Bicara Therapeutics Inc(BCAX)COM055477103$16.3M550,4082.3%
Caredx Inc(CDNA)COM14167L103$15.2M531,8702.1%
Celldex Therapeutics Inc(CLDX)COM NEW15117B202$14.9M399,8562.1%
Compass Therapeutics Inc(CMPX)COM20454B104$12.8M5,831,8131.8%
Alkermes PLC(ALKS)SHSG01767105$12.7M242,5601.8%
First Tracks Biotherapeutics(TRAX)ORD SHS337185102$12.1M603,4891.7%
Prothena Corp PLC(PRTA)SHSG72800108$11.2M1,143,1551.5%
Travere Therapeutics Inc(TVTX)COM89422G107$9.5M167,5251.3%
Taysha Gene Therapies Inc(TSHA)COM SHS877619106$9.5M1,391,3821.3%
Aclaris Therapeutics Inc(ACRS)COM00461U105$8.5M1,613,4301.2%
Agios Pharmaceuticals Inc(AGIO)COM00847X104$7.9M213,6011.1%
Capricor Therapeutics Inc(CAPR)COM NEW14070B309$5.5M229,7630.8%
Align Technology Inc(ALGN)COM016255101$5.3M31,3890.7%
Oruka Therapeutics Inc - Restricted(ORKA)COM687604108$3.2M33,5460.4%
Xenon Pharmaceuticals Inc(XENE)COM98420N105$3.1M51,3450.4%
Neurocrine Biosciences Inc(NBIX)COM64125C109$3.1M18,1170.4%
Edwards Lifesciences Corp(EW)COM28176E108$3.0M33,6400.4%
Stoke Therapeutics Inc(STOK)COM86150R107$2.8M84,6310.4%
Cytokinetics Inc(CYTK)COM NEW23282W605$2.7M32,1950.4%
Pyxis Oncology Inc(PYXS)COMMON STOCK747324101$2.6M864,2770.4%
Ehealth Inc(EHTH)COM28238P109$2.2M1,482,7970.3%
Crispr Therapeutics AG(CRSP)NAMEN AKTH17182108$2.2M39,6050.3%
Sagimet Biosciences Inc(SGMT)COM SER A786700104$1.9M250,0000.3%
Nuvation BIO Inc(NUVB)COM CL A67080N101$1.9M326,6090.3%
Biontech SE(BNTX)SPONSORED ADS09075V102$1.8M19,6140.3%
Compass Pathways PLC ADR(CMPS)SPONSORED ADS20451W101$1.6M115,6160.2%
Humana Inc(HUM)COM444859102$1.6M3,9850.2%
Newamsterdam Pharma Co NV(NAMS)ORDINARY SHARESN62509109$1.5M44,3590.2%
Verastem Inc(VSTM)COM NEW92337C203$1.2M309,6850.2%
Madrigal Pharmaceuticals Inc(MDGL)COM558868105$959.5K1,7870.1%
Urogen Pharma LTD(URGN)COMM96088105$901.6K24,5000.1%
Bicycle Therapeutics PLC(BCYC)SPONSORED ADS088786108$856.0K201,8900.1%
Xeris Biopharma Holdings Inc(XERS)COM98422E103$826.9K104,4100.1%
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